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U7snRNA-mediated Exon 17 Skipping Restores Dystrophin Expression in Cells and in a Novel Mouse Model of Duchenne Muscular Dystrophy

L. Gushchina,G. Dufresne, E. Saylam,A. Bradley,N. Rohan, A. Lowery, A. Suhaiba, H. Lin,N. Wein,K. Flanigan

NEUROMUSCULAR DISORDERS(2024)

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