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Insights into the Effects of Subretinal Voretigene Neparvovec-Rzyl in RPE65-associated Leber Congenital Amaurosis

Alaa Tayyib, Deepika C. Parameswarappa, Peter J. Kertes,Rajeev Muni,Anupreet Tumber,Gregory Costain, Alex Schramm, Heather MacDonald,Regan Klatt,Ajoy Vincent,Elise Héon

Canadian Journal of Ophthalmology(2025)

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