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Intra-CSF AAV9-GBA Delivery Produces Species and Route of Administration Differences in Safety and Efficacy

Neeta Abraham, Ana Amaral, Shawn Kyle Bourque, Yi Chen,Pete Clarner, Jim Fikes, Peter-Joseph De Giovanni,Davide Gianni, Kelly E. Glajch,Branka Grubor,Stefan Hamann, Warren Hirst,Melissa Kirkland, Lee Koetzer, Merilla Michael, Prasad Nadella,Kalyani Nambiar, Ed Plowey,Jennifer Sebalusky,Junghae Suh,Eric Tien,Patrick Trapa, Dominic Walsh,Shanqin Xu, Weike Zeng

MOLECULAR THERAPY(2024)

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