Long-Term Safety and Urea Cycle Function Following a Phase 1/2 Trial of DTX301 in Adults with Late-Onset Ornithine Transcarbamylase (OTC) DeficiencyCary O. Harding,Tarekegn Geberhiwot,Maria Luz Couce,Nathalie Guffon,Wen-Hann Tan, Leticia Ceberio Hualde,Aneal Khan,Laura Konczal,Janet A. Thomas, Margo Sheck Breilyn,Lin Zhang,J. Lawrence Merritt,Eric CrombezMOLECULAR THERAPY(2024)引用 0|浏览4AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要