Durable Clinical Benefits with Exagamglogene Autotemcel for Severe Sickle Cell Disease
Haydar Frangoul,Franco Locatelli,Akshay Sharma,Monica Bhatia,Markus Y Mapara,Robert I. Liem,Donna Wall,Lyndsay Molinari,Laurence Dedeken,Kevin H.M. Kuo,Paul Telfer,Ami J. Shah,Marina Cavazzana,Selim Corbacioglu,Michael J. Eckrich,Damiano Rondelli,Roland Meisel,Stephan Lobitz,Mariane De Montalembert,Martin H. Steinberg,Mark C. Walters, Laura Bower,Suzan Imren, Tina Liu, Weiyu Zhou,William Hobbs,Stephan A. Grupp Blood(2024)
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