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Rapid, Efficient and Durable Fetal Hemoglobin Production Following CS-101 Treatment in Transfusion-Dependent Β-Thalassemia Participants: an Autologous, Ex Vivo Edited CD34+ Stem Cell Product Using the Innovative Transformer Base Editor (Tbe)

Yongrong Lai,Rongrong Liu, Lijie Wang, Xu-Kai Ma, Yaliang Li,Gaohui Yang,Lingling Shi, Jia Wei,Zhenbin Wei,Xuemei Zhou, Kewei Lan, Yan Zhang, Xiaodun (Susan) Mou,Li Yang,Jia Chen

Blood(2024)

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