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699P Exon Skipping for the Second Calponin Homology Domain of Dystrophin Using AAV.U7snRNA - in Vitro & Intramuscular Studies Using a Novel Murine Model of Duchenne Muscular Dystrophy

A. Brinkman,D. Lesman,D. Li,D. Rajakumar, C. Atre,Y. Rodriguez, C. Almeida,N. Wein

Neuromuscular Disorders(2024)

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