Anti-human-TfR-GAA efficiently clears CNS and muscle glycogen in a translatable hTfR-KI/Pompe disease mouse model
Arjan van der Flier,Raquel Riley,Laurie Smith,Sofia Kinton,Shan Zhou,Elena Kistanova,Renee Bodinizzo,Lilu Guo,Colleen Maloney,Caroline Morel,Dinesh S. Bangari,Kristina An Haack,Kelly George
