Chrome Extension
WeChat Mini Program
Use on ChatGLM
VIPCreated with Sketch.

20 Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)

Morna Dorsey,Manish Butte, Jay Lieberman,Heather Lehman,Tracy Fausnight,Michael Keller,Caroline Fradette,Michael Hershfield,Tamara Pozos,Anna Rozova,Luke Wall,M. Teresa de la Morena,Jeffrey Bednarski,Teresa Tarrant,Hey Chong,Bob Geng,Noemi Toiber Temin,Susan Laubach, Leo Lin,Talal Mousallem

Clinical Immunology（2024）

Cited 0|Views17
No score
Key words
ADA-SCID,Enzyme replacement therapy,Adenosine deaminase severe combined immunodeficiency,HSCT,Registry,Immunodeficiency
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined