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Delphi Consensus Panel on Assessing Clinically Meaningful Treatment Outcomes in Adults Living with Spinal Muscular Atrophy (SMA) (P2-11.007)

Kate Sully,Claudia Chiriboga,Tina Duong,Yasemin Erbas, Jacqueline Glascock,Nicole Gusset,Robert Muni-Lofra, Colleen O’Connell,Juan F. Vázquez-Costa,Maggie C. Walter, Carol Jean Guittari,James Cochrane,Louisa D. Townson, Jason Kufakwaro, Anne Marciniak,Danielle Riley,Julian Nam

Neurology(2024)

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