Splice-switching oligonucleotides as therapeutics for citrin deficiency patients with a novel deep intronic variantKimihiko Oishi,Jin Rong Ow,Eri Imagawa, Wei Yuan Cher, Venkataramanan Ramadass,Tommaso Tabaglio,Manikandan Lakshmanan,Ernesto Guccione,Keng Boon WeeMolecular Genetics and Metabolism(2024)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要