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Motor function limitations and impacts among patients with GM1 AND GM2 gangliosidoses in the United States: A qualitative study

Daisy Ng-Mak, Maria Belen Rodriguez,Karli Heuer, Christine Waggoner, Diana Jussila,Ruth Pulikottil-Jacob, Nancy Gabriela Perez,Robert Krupnick

Molecular Genetics and Metabolism(2024)

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