Innovative Transformer Base Editor (tBE)-Mediated Editing at BCL11A Binding Motif Triggers High Level of -Globin Expression with No Observable Off-Target MutationsJia Chen,Wenyan Han,Hou-Yuan Qiu,Shangwu Sun,Zhi-Can Fu, Guo-Quan Wang,Li Yang,Bei Yang,Ying ZhangBLOOD(2023)引用 0|浏览6暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要