Treatment of Congenital Hypotransferrinemia Patients with Human Apotransferrin Resolves Anemia and Reduces Iron Accumulation

Ilona Kleine Budde, Cristina Díaz De Heredia,Raffaella Mariani,Alberto Piperno,Katja Moser,Mayka Sanchez,Thomas Bodewes, Maya Isaila

Blood(2023)

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