VP369 Disease burden, treatment patterns and healthcare resource utilization associated with Pompe disease in Sweden: a real-world evidence study

C. Lindberg, S. Nordin, M. Stelmaszuk,A. MacCulloch, R. Graham, A. Ekström, B. Lindvall,J. Freilich

Neuromuscular Disorders(2023)

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关键词
pompe disease,healthcare resource utilization,treatment,real-world
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