Transplantation Using Targeted Busulfan for Diamond–Blackfan Anemia

Pediatrics InternationalVolume 65, Issue 1 e15440 CLINICAL NOTE Transplantation using targeted busulfan for Diamond–Blackfan anemia Shota Kato, Shota Kato orcid.org/0000-0003-3656-2665 Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorYoshiko Nakano, Yoshiko Nakano Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Department of Cell Therapy and Transplantation Medicine, The University of Tokyo Hospital, Tokyo, JapanSearch for more papers by this authorMoe Hidaka, Moe Hidaka Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Department of Cell Therapy and Transplantation Medicine, The University of Tokyo Hospital, Tokyo, JapanSearch for more papers by this authorMasahiro Sekiguchi, Masahiro Sekiguchi Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorKentaro Watanabe, Kentaro Watanabe Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorJunya Fujimura, Junya Fujimura Department of Pediatrics, Juntendo University Faculty of Medicine, Tokyo, JapanSearch for more papers by this authorMotohiro Kato, Corresponding Author Motohiro Kato [email protected] orcid.org/0000-0001-5145-1774 Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Correspondence Motohiro Kato, Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, 7-3-1 Hongo, Bunkyo-Ku, Tokyo 113-8655, Japan. Email: [email protected]Search for more papers by this author Shota Kato, Shota Kato orcid.org/0000-0003-3656-2665 Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorYoshiko Nakano, Yoshiko Nakano Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Department of Cell Therapy and Transplantation Medicine, The University of Tokyo Hospital, Tokyo, JapanSearch for more papers by this authorMoe Hidaka, Moe Hidaka Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Department of Cell Therapy and Transplantation Medicine, The University of Tokyo Hospital, Tokyo, JapanSearch for more papers by this authorMasahiro Sekiguchi, Masahiro Sekiguchi Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorKentaro Watanabe, Kentaro Watanabe Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, JapanSearch for more papers by this authorJunya Fujimura, Junya Fujimura Department of Pediatrics, Juntendo University Faculty of Medicine, Tokyo, JapanSearch for more papers by this authorMotohiro Kato, Corresponding Author Motohiro Kato [email protected] orcid.org/0000-0001-5145-1774 Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, Tokyo, Japan Correspondence Motohiro Kato, Department of Pediatrics, Graduate School of Medicine, The University of Tokyo, 7-3-1 Hongo, Bunkyo-Ku, Tokyo 113-8655, Japan. Email: [email protected]Search for more papers by this author First published: 10 December 2022 https://doi.org/10.1111/ped.15440Read the full textAboutPDF ToolsRequest permissionExport citationAdd to favoritesTrack citation ShareShare Give accessShare full text accessShare full-text accessPlease review our Terms and Conditions of Use and check box below to share full-text version of article.I have read and accept the Wiley Online Library Terms and Conditions of UseShareable LinkUse the link below to share a full-text version of this article with your friends and colleagues. Learn more.Copy URL Share a linkShare onEmailFacebookTwitterLinkedInRedditWechat No abstract is available for this article. CONFLICT OF INTEREST The authors declare no conflict of interest. REFERENCES 1Diaz-de-Heredia C, Bresters D, Faulkner L, Yesilipek A, Strahm B, Miano M, et al. Recommendations on hematopoietic stem cell transplantation for patients with diamond–Blackfan anemia. On behalf of the pediatric diseases and severe aplastic anemia working parties of the EBMT. Bone Marrow Transplant. 2021; 56: 2956–63. 2Koyamaishi S, Kamio T, Kobayashi A, Sato T, Kudo K, Sasaki S, et al. Reduced-intensity conditioning is effective for hematopoietic stem cell transplantation in young pediatric patients with diamond–Blackfan anemia. Bone Marrow Transplant. 2021; 56: 1013–20. 3Matsumoto K, Uchida N, Sakurai A, Taniguchi S, Morita K. Clinical application of the dried blood spot method in the measurement of blood Busulfan concentration. Biol Blood Marrow Transplant. 2016; 22: 1968–73. 4Osumi T, Tomizawa D, Kawai T, Sako M, Inoue E, Takimoto T, et al. A prospective study of allogeneic transplantation from unrelated donors for chronic granulomatous disease with target busulfan-based reduced-intensity conditioning. Bone Marrow Transplant. 2019; 54: 168–72. 5Jacobsohn DA, Duerst R, Tse W, Kletzel M. Reduced intensity haemopoietic stem-cell transplantation for treatment of non-malignant diseases in children. Lancet. 2004; 364: 156–62. Volume65, Issue1January/December 2023e15440 ReferencesRelatedInformation