Eladocagene exuparvovec gene therapy improves motor development in patients with aromatic L-amino acid decarboxylase deficiency

P. Hwu, J. Sierra,Y-H Chien,N-C Lee,A. Wang,J. Turna, V Penematsa, L. Golden,C-H Tai

ANNALS OF NEUROLOGY(2023)

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关键词
Neurodevelopmental Disorders, Neurometabolic
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