Long-term efficacy and safety of elivaldogene autotemcel (eli-cel) gene therapy: an integrated analysis of 67 patients with cerebral adrenoleukodystrophy (CALD)

F. Eichler, C. Duncan,J-S Kuhl,S. De Oliveira, A. Thrasher, J-H Dalle, C. Sevin,A. Shah, F. Locatelli, H. Amartino, M. Engelen, G. Downey, A. Dietz, P. Orchard,D. Williams, Himal Thakar

ANNALS OF NEUROLOGY（2023）

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