AAV5-miHTT gene therapy mediates sustained mutant huntingtin lowering in brain and cerebrospinal fluid of Huntington's disease minipigs up to 5 years L. van der Bent, C. Brouwers,A. Stam, L. Spronck, J. Klima, J. Juhasova, B. Levinska,S. Juhas, J. Motlik,M. Evers, Z. Ellederova,A. VallesMOVEMENT DISORDERS(2023)引用 0|浏览7暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要