RNA Base Editing for the Treatment of Alpha-1 Antitrypsin Deficiency
Prashant Monian,Chikdu Shivalila,Genliang Lu,Keith Bowman, Marissa Bylsma,Michael Byrne,Megan Cannon,Jigar Desai, Alyse Faraone,Frank Favaloro,Anamitra Ghosh,Jack Godfrey, Nidia Hernandez,Naoki Iwamoto,Tomomi Kawamoto,Jayakanthan Kumarasamy,Pachamuthu Kandasamy,Anthony Lamattina,Muriel Lemaitre,Amber Lindsey,Fangjun Liu,Richard Looby,Khoa Luu,Jake Metterville,Ik-Hyeon Paik,Qianli Pan, Tom Pu,Erin Purcell-Estabrook, Jeanette Rheinhardt,Mamoru Shimizu,Kuldeep Singh,Stephany Standley, Carina Th Omas,Snehlata Tripathi,Hailin Yang, Ryan Yordanoff,Yuan Yin, Hui Yu,Padma Narayanan,Paloma H. Giangrande,Chandra Vargeese MOLECULAR THERAPY(2023)
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