Small Nuclear RNA-Mediated Exon 51 Skipping AAV9 Gene Therapy for the Treatment of Duchenne Muscular Dystrophy
Rea Lardelli Markmiller,Greg Nachtrab,Claire Geddes, Taka Tadokoro, Sheik Pasha, Daniel Knowland,Daniela Roth, Alberto Carreno, Gustavo Villegas,Anindita Sarkar, Derek Reid, Lynn Nguyen, Rachel Adams, Oscar Diago, Shruti Vakharia, Bryan Almaguer,Haydee Gutierrez, Yesol Go,Ronald Torres,Nandini Narayan, Deepti Vashist, Aaron Berlin, Amanda Tran,Ranjan Batra,John E. Leonard MOLECULAR THERAPY（2023）
AI 理解论文
溯源树
样例
