In Vivo Selection in Non-Human Primates Identifies AAV Capsids Having Enhanced Transgene Expression and Biodistribution in Spinal Cord after Intrathecal Administration

Casey A. Maguire,Killian S. Hanlon, Karen Kozarsky,Sean Clark, Yi Gong, Ming Cheng, Demitri De la Cruz,Nikita Patel, Miguel Santoscoy, Diane M. Nguyen,Josette Nammour

MOLECULAR THERAPY(2023)

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