Engineering Human Hematopoietic Stem and Progenitor Cells for Lineage-Specific Expression of Galactocerebrosidase Using Genome Editing Nelson A. Amorin, Lexi-Ann Golden,Edina Poletto, Nicole Marie Johnston, William Feist, Talia Menezes, Karen Kikuta,Sofia Elena Luna, Celia Charlton,Tyler Kashuv,Natalia Gomez-OspinaMOLECULAR THERAPY(2023)引用 0|浏览4暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要