Exceptional Fetal Hemoglobin Induction by BCL11A+58/+55 Combined Enhancer Editing and Hydroxyurea Treatment in Rhesus Monkeys
Selami Demirci,Jing Zeng,Khaled Essawi,Anh Nguyen,Ulana Stasula,Rebecca Chu,Alexis Leonard,Shaina N. Porter, Muhammad B. N. Khan, Gabriela Hinojosa,Naoya Uchida,Cicera R. Lazzarotto,Stacy A. Maitland,Aylin C. Bonifacino,Allen E. Krouse, Nathaniel S. Linde,Robert E. Donahue,Shengdar Q. Tsai,Shondra Pruett-Miller,Scot A. Wolfe,Daniel E. Bauer,John F. Tisdale MOLECULAR THERAPY(2023)
AI 理解论文
溯源树
样例