Cell-Type Specific Reduction of Prion Expression in Neurons and Astrocytes Using Engineered Zinc Finger Transcriptional Regulators

Victoria Shih-Wei Chou,Kimberly Marlen, Qi Yu, Giulia Cisbani, Finn Peters, Garrett Lew, Meredith Mortberg, Chiara Melis, Finn Hartstein, Jing Hu, Swetha Garimalla, David Ojala,Sarah Hinkley,Alicia Goodwin, Mohad Mehrabian,Eric Vallabh Minikel,Sonia M. Vallabh,Amy Pooler,Bryan Zeitler

MOLECULAR THERAPY(2023)

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