Reversal of Cardiac Phenotype in a Mouse Model of Friedreich's Ataxia Following Administration of AAV Gene Therapy
Joshua C. Chang,Whitney Blankenberger,Su Liu,Marie Stark,Jacqueline A. Brassard,Tianbi Zhang,Fria Bolan,Samuel D. Sutton,Mario Guerrero,Jose A. Corleto,Nakyo Heo,Dwaipayan Sen,Mark A. Champe,Fabrizia Urbinati,Bala Medicherla,Carlos Fonck