Intracerebroventricular Delivery of SLC6A8 by Self Complimentary AAV9 Restores Brain Creatine and Reduces Hyperactivity in a Mouse Model of SLC6A8 Deficiency

Troy B. Webster, Robyn T. Binsfeld,Ilona Tkachyova, Andreas Schulze,Jagdeep S. Walia,Steven Gray

MOLECULAR THERAPY(2023)

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