Development of a Human PCSK9-Targeting Epigenetic Editor with Durable, Near-Complete in Vivo Silencing Efficiency
Frederic Tremblay, Kenneth Kelly, Shrijal Shah, Gabriel El Sebae,Scott Clarkson, Thijs Udo, Kendra Bayne, Melissa Pannone, Liam Lofgren, Tess Sevetson,Sahar Abubucker, Ricardo Ramirez,Erica Hildebrand, Christina Tarr, Narayan Wong,Kuo-Chan Hung, Zohan Hoque, Kusha Chopra, Shane Wright,Morgan L. Maeder,Mary Morrison,Angus Li,Mehana Daftary,Ari E. Friedland, David Litvak, Catherine Stehman-Breen,Martino Alfredo Cappelluti,Angelo Lombardo, Pietro Spinelli,Cecilia Fernandez,John Xiong,Vic Myer, Aron B. Jaffe MOLECULAR THERAPY(2023)
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