Liver-Directed Lentiviral Gene Therapy is Safe and Curative in Argininosuccinic AciduriaLoukia Touramanidou,Sonam Gurung, Hu Yi-Ting,Dany P. Perocheau,Simon N. Waddington,John R. Counsell,Adrian J. Thrasher,Paul Gissen,Giandomenico Turchiano,Julien BaruteauMOLECULAR THERAPY(2023)引用 0|浏览12暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要