Nonclinical Pharmacology, Biodistribution, and Safety Studies Supporting the Clinical Development of DB-OTO (AAV1-Myo15-hOTOFv5) for Hearing Loss Due to Genetic Otoferlin Protein DeficiencyChristopher Thompson, Seth Koehler,Ning Pan,Lars Becker,Quynh-Anh Fucci,Xichun Zhang,Joseph Goodliffe,Tyler M. Gibson, Janet Chung, Peter Slade, Orion Keifer,Peter Weber,Eduardo Corrales,Kathy So,Yoojin Chung,Sarah Cancelarich,Danielle Velez,Leah Sabin,Meghan Drummond, Yamini Patel,Jonathan Weyne, Courtney Shanks,Joseph Burns, John Lee,Adam Palermo,Jonathon Whitton,Vassili ValayannopoulosMOLECULAR THERAPY(2023)引用 0|浏览8暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要