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IGAm: A novel index predicting long-term survival in patients with early-diagnosed inherited metabolic disorders.

Journal of pediatric endocrinology & metabolism : JPEM(2023)

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摘要
The devised novel IGAm index can predict long-term survival in patients with IMDs, with a high IGAm index being associated with higher mortality in patients with IMDs.
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关键词
inherited metabolic disorders, mortality, long-term survival, index
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