Safety and efficacy of arimoclomol for inclusion body myositis: a multicentre, randomised, double-blind, placebo-controlled trial.

The Lancet. Neurology(2023)

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摘要
US Food and Drug Administration Office of Orphan Products Development and Orphazyme.
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关键词
inclusion body myositis,arimoclomol,double-blind,placebo-controlled
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