Identification and Optimization of RNA-Splicing Modulators As Huntingtin Protein-Lowering Agents for the Treatment of Huntington's Disease.
Longbin Liu,Karine Malagu,Alan F. Haughan,Vinod Khetarpal,Andrew J. Stott,William Esmieu,Huw D. Vater, Stephen J. Webster,Amanda J. van de Poel,Cole Clissold,Brett Cosgrove, Benjamin Sutton,Jonathan A. Spencer,Perla Breccia,Emanuela Gancia, Silvia Bonomo,Tammy Ladduwahetty,Ovadia Lazari,Hiral Patel, Helen C. Atton,Steve Clifton, Daniel M. Mota, Dario Magnani, Amy O'Neill,Marta Stebbeds,Natsuko Macabuag,Daniel Todd, Maria E. Herva,Philip Mitchell,Mijke Visser, Sara Compte Sancerni,Laure Grand Moursel, Marta da Silva, Eva Kritikou,Taneli T. Heikkinen, Tamuna Bolkvadze,Valentina Fodale, Debora Spadafora,Manuel Daldin,Alberto Bresciani,John E. Mangette,Elizabeth M. Doherty,Matthew R. Lee,Todd Herbst,Edith Monteagudo,Douglas Macdonald,Nikolay V. Plotnikov,Mark Chambers,George Mcallister,Ignacio Munoz-Sanjuan,Celia Dominguez JOURNAL OF MEDICINAL CHEMISTRY（2023）
关键词
Gene Expression Dysregulation
AI 理解论文
溯源树
样例
