Safety and efficacy of the epithelial sodium channel blocker idrevloride in people with primary ciliary dyskinesia (CLEAN-PCD): a multinational, phase 2, randomised, double-blind, placebo-controlled crossover trial

The Lancet. Respiratory medicine(2024)

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摘要
Parion Sciences, under agreement with Vertex Pharmaceuticals.
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关键词
primary ciliary dyskinesia,sodium channel,clean-pcd,double-blind,placebo-controlled
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