SMN2 Gene Splicing Modifiers Restore Lifespan and Motor Behavior in a Mouse Model of Spinal Muscular Atrophy.
Nikolai A. Naryshkin,Marla Weetall,Amal Dakka,Jana Narasimhan,Xin Zhao,Zhihua Feng, Karen Ling,Gary M. Karp,Hongyan Qi,Matthew G. Woll,Guangming Chen,Nanjing Zhang,Vijayalakshmi Gabbeta,Priya Vazirani,Anuradha Bhattacharyya,Bansri Furia,Nicole Risher,Josephine Sheedy,Ronald Kong, Jiyuan, Jiaxin Ma,Anthony Turpoff,Chang-Sun Lee,Xiaoyan Zhang,Young‐Choon Moon,Panayiota Trifillis,Ellen Welch,Joseph M. Colacino,John Babiak,Neil G. Almstead,Stuart W. Peltz, Loren A. Eng,Karen S. Chen,Jesse L. Mull,Maureen S. Lynes,Lee L. Rubin,Paulo Fontoura,Luca Santarelli,Daniel Haehnke,Kathleen McCarthy,Roland Schmucki,Martin Ebeling,Manaswini Sivaramakrishnan,Chien‐Ping Ko,Sergey Paushkin,Hasane Ratni,Irene Gerlach,Anirvan Ghosh,Friedrich Metzger openalex(2014)
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