Liver Directed Lentiviral Gene Therapy Provides Long Term Phenotypic Correction of Methylmalonic Acidemia in a Mouse ModelElena Barbon,Camilla Negri,Andrea Raimondi,Chiara Simoni,Francesca Sanvito,Anna Fabiano,Fabio Russo,Alessio CantoreHUMAN GENE THERAPY(2023)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要