Chemically surface modified AAV6 vectors combined with nanoblades are a promising alternative for gene knock-in in HSCs

A. Gutierrez-Guerrero, A. Leray, S. Perian, D. Alvarez-Dorta,E. Ayuso,F. L. Cosset, D. Deniaud,M. Mevel, E. Verhoeyen

HUMAN GENE THERAPY(2022)

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