Safety assessment of gene edited CD4(+) T-cells for the treatment of Hyper-IgM 1

D. Canarutto, V. Vavassori,S. Ferrari, T. Plati, S. Porcellini, C. Asperti, M. Radrizzani,M. Paulis, A. Villa,L. Naldini

HUMAN GENE THERAPY(2022)

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