Therapeutic Gene Editing of HSCs Ex Vivo without in Vitro Culture Avoids Genotoxicity, Simplifies Procedures, and Preserves Efficiency and Stemness
Jing Zeng,My Anh Nguyen,Marioara-Felicia Ciuculescu,Esther Mintzer,Pengpeng Liu,Linda Yingqi Lin,Tolulope O Rosanwo,Archana Verma, Nola Neri,Stacy A. Maitland,Alden Richter,David G. Justus,Kendell Clement,Christian Brendel,Luca Pinello,John P Manis,Myriam Armant,Scot A. Wolfe,Daniel E. Bauer Blood(2022)
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