WS16.03 LUNAR-CF: an mRNA replacement approach for cystic fibrosis lung disease

D. Geller, C.G. Perez-Garcia,Y. Pei, X. Liu,J. Engelhardt,C. Hodges, M. Mense, K. Coote,Y. Cheng, J.E. Mahoney, S. Parker,P. Chivukula

Journal of Cystic Fibrosis(2022)

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cystic fibrosis,mrna replacement approach
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