Identification and Characterization of a MAPT-targeting Locked Nucleic Acid Antisense Oligonucleotide Therapeutic for Tauopathies
Molecular Therapy — Nucleic Acids(2022)
关键词
MT: oligonucleotides: therapies and applications,MAPT,tau,tauopathies,neurodegeneration,antisense oligonucleotides,locked nucleic acids,cynomolgus monkey,intrathecal
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