In Vitro Modeling and Rescue of Ciliopathy Associated with IQCB1/NPHP5 Mutations Using Patient-Derived Cells
Stem Cell Reports（2022）
Key words
patient-derived iPSC,retinal organoids,photoreceptor,primary cilia,gene therapy,vision,Leber congenital amaurosis,Senior-Løken syndrome,stem cells,RPE
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined