Lentiviral-mediated gene therapy for patients with fanconi anemia [group a]: updated results from global rp-l102 clinical trials
Julian Sevilla,Claire Booth,Agnieszka Czechowicz,Rajni Agarwal,Josune Zubicaray,Paula Rio,Kritika Chetty, Grainne O'Toole,Jinhua Xu-Bayford,Philip Ancliff,Elena Sebastian,Grace Choi, Miriam Zeini, Eileen Nicoletti,Cindy Eide,John Wagner,Gayatri Rao,Adrian Thrasher,Jonathan Schwartz,Maria Grazia Roncarolo, Juan Bueren MOLECULAR THERAPY(2023)
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fanconi anemia,gene therapy,clinical trials,lentiviral-mediated
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