Low-density lipoprotein (LDL) receptor liver gene transfer with lentiviral vectors achieves full normalization of LDL cholesterol and protection from atherosclerosis in a mouse model of familial hypercholesterolemia

C. Canepari,M. Milani,F. Russo, F. Starinieri, R. Norata, M. Rocchi,M. Biffi,A. Fabiano, F. Sanvito,A. Cantore

MOLECULAR THERAPY(2022)

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