A Mutation-Independent CRISPR/Cas9-Based `Knockout and Replace' Strategy to Treat Rhodopsin-Associated Autosomal Dominant Retinitis Pigmentosa

Chi-Hsiu Liu, Pavlina Wolf, Ruhong Dong, Yan Huang,Diana Tabbaa,Eugenio Marco, Brian Duke,Andrea Pinilla,Asha Pant,Racheal D'Souza, Judith Newmark,Georgia Giannoukos,Kate Zhang,Adrian Timmers,Mark S. Shearman, Mariacarmela Allocca

MOLECULAR THERAPY(2022)

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