Adeno-Associated Virus Mediated SGPL1 Gene Therapy as a Treatment for Sphingosine Phosphate Lyase Insufficiency Syndrome (SPLIS)Julie Saba,Piming Zhao,Gizachew Tassew,Joanna Lee,Babak Oskouian, Denise Munoz, Jeffrey B. Hodgin,Gordon L. Watson, Felicia Tang,Jen-Yeu Wang,Jinghui Luo,Yingbao Yang, Sarah King,Ronald KraussMOLECULAR THERAPY(2022)引用 0|浏览6暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要