Long-Term Phenotypic Correction of Fanconi Anemia-A Patients Treated by Gene Therapy in Early Stages of the Bone Marrow Failure
Paula Rio,Julian Sevilla,Susana Navarro,Josune Zubicaray,Rebeca Sanchez-Dominguez,Eileen Nicoletti,Wei Wang,Roser M. Pujol,Michael Rothe,Jose C. Segovia,Rosa M. Yanez,Jose A. Casado,Yari Gimenez,Omaira Alberquilla,Elena Almarza,Jordi Barquinero,Nagore Garcia de Andoin,Ricardo Lopez,Albert Catala,Francois Lefrere,Marina Cavazzana,Manfred Schmidt,Axel Schambach,Gayatri Rao,Jordi Surralles,Jean Soulier,Cristina Diaz de Heredia,Jonathan D. Schwartz,Juan A. Bueren MOLECULAR THERAPY(2022)
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