Safety and Outcomes of Intravenous scAAV9.U7-ACCA for the Treatment of Duchenne Muscular Dystrophy Caused by Exon 2 DuplicationsMegan A. Waldrop,Michael W. Lawlor,Tatyana Vetter,Emma C. Frair,Margaret J. Beatka,Hui Meng,Megan A. Iammarino, Brenna Sabo,Sharmada Subramanian, Kristen Brown,Maryann Kaler,Tabatha Simmons,Kim McBride,Nicolas Wein,Kevin M. FlaniganMOLECULAR THERAPY(2022)引用 0|浏览9暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要