Clinical trial update: Ex-vivo autologous hematopoietic stem cell gene therapy in MPS IIIASimon A. Jones,Jane L. Kinsella,Jane Potter,Adrian Thrasher,Claire Booth,Karen Buckland,Natalia Izotova,Stewart Rust,Daniel Weisberg,Heather Church,Karen Tylee,Helena Lee,Laura Ford,Rebecca J. Holley,Stuart Ellison,Brian W. Bigger,Robert F. WynnMOLECULAR GENETICS AND METABOLISM(2022)引用 0|浏览11暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要