Outcomes after Hematopoietic Cell Transplant and Gene Therapy for Adenosine Deaminase (ADA) Severe Combined Immune Deficiency: A Combined Analysis from the Primary Immune Deficiency Treatment Consortium (PIDTC) 6901 and 6902 Studies Geoff D.E. Cuvelier , Brent Logan , Susan E. Prockop , Rebecca H. Buckley , Caroline Y. Kuo , Linda M. Griffith , Xuerong Liu , Alison Yip , Michael S. Hershfield , Roberta E Parrott , Christen L. Ebens , Theodore B. Moore , Richard J. O’Reilly , Sung-Yun Pai , Malika Kapadia , Neena Kapoor , Lisa R. Forbes Satter , Caridad Martinez , Lauri M. Burroughs , Aleksandra Petrovic , Monica S. Thakar , Deepak Chellapandian , Jennifer Heimall , David C. Shyr , Ahmad Rayes , Jeffrey J. Bednarski II , Sharat Chandra , Shanmuganathan Chandrakasan , Alfred P. Gillio , Lisa Madden , Troy C. Quigg , Emi H. Caywood , Blachy J Dávila Saldaña , Kenneth DeSantes , Hesham Eissa , Frederick Goldman , Jacob Rozmus , Ami J Shah , Mark T. Vander Lugt , Mike A. Pulsipher , Luigi D. Notarangelo , Morton J. Cowan , Christopher C. Dvorak , Elie Haddad , Jennifer Puck , Donald B. Kohn Transplantation and Cellular Therapy(2022)
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